E-BOOK: Gene Therapies of the Eye Preclinical Reference Guide

This e-book aims to overview cell and gene therapies for ocular diseases from a preclinical drug development perspective. We provide descriptions of current best practices in the use of model systems, preclinical development, and study design, as well as guiding principles for regulatory approval. Finally, we discuss our view about how the sector is likely to evolve in the coming decade.

Are you prepared for the preclinical challenges involved in developing gene therapies of the eye?